In a $12 billion deal, Novartis has agreed to acquire Avidity Biosciences, which is developing several treatments for ...

As columnist Robin Stemple's FSHD progresses, he worries about how his increased care needs will affect his family caregivers ...

Bridgebio Pharma says it will seek U.S. approval of BBP-418 for LGMD2i after Phase 3 trial data showed a range of benefits ...

Learn how Duchenne muscular dystrophy affects oral health and explore tips for daily care, dental visits, and preventing ...

Use of the oral therapy BBP-418 appeared to improve walking ability and lung function in people with limb-girdle muscular dystrophy type 2i (LGMD2i) — characterized by muscle wasting at the shoulders ...

Learning how to talk to doctors about Duchenne muscular dystrophy can help support you in your role as a caregiver for someone with DMD.

Duchenne muscular dystrophy can increase the risk of pressure sores, but practical strategies can help in preventing skin ...

DMD treatment Agamree works differently from traditional corticosteroids, blocking the action of a receptor, a study found.

Advocating for Duchenne MD doesn't just mean testifying in Washington, D.C.. It also means giving what you can, says columnist.

Brogidirsen shows motor benefits and safety over 3.5 years of treatment in people with DMD who are amenable to exon 44 ...

Feeling discouraged by the progression of his FSHD, columnist Robin Stemple focuses on the love and kind gestures he's ...

Three boys with DMD given the gene therapy GNT0004 in a trial showed sustained improvements in motor function after two years ...